PUBLICATIONS
Ryckman AE, Deschenes NM, Quinville BM, Osmon KJL, Mitchell M, Chen Z, Gray SJ, Walia JS.
Characterization of a phenotypically severe animal model for human AB-Variant GM2 gangliosidosis.
Deschenes NM, Cheng C, Khanal P, Quinville BM, Ryckman AE, Mitchell M, Pshezhetsky AV, Walia JS.
Vyas M, Deschenes NM, Osmon KJL, Chen Z, Ahmad I, Kot S, Thompson P, Richmond C, Gray SJ, Walia JS.
Biochemical Correction of GM2 Ganglioside Accumulation in AB-Variant GM2 Gangliosidosis
Deschenes NM, Cheng C, Ryckman AE, Quinville BM, Khanal P, Mitchell M, Chen Z, Sangrar W, Gray SJ, Walia JS
Gene Expression Profile in the Sandhoff Mouse Brain with Progression of Age.
Singh K, Quinville BM, Mitchell M, Chen Z, Walia JS.
Quinville BM, Deschenes NM, Ryckman AE, Walia JS.
Ryckman AE, Brockhausen I, Walia JS.
Efficacy of a Bicistronic Vector for Correction of Sandhoff Disease in a Mouse Model
Woodley E, Osmon KJL, Thompson P, Richmond C, Chen Z, Gray SJ, Walia JS.
Osmon KJ, Vyas M, Woodley E, Thompson P, Walia JS.
Osmon KJ, Woodley E, Thompson P, Ong K, Karumuthil-Melethil S, Keimel JG, Mark BL, Mahuran D, Gray SJ, Walia JS.
Kamel D, Gray C, Walia JS, Kumar V.
Karumuthil-Melethil S, Nagabhushan Kalburgi S, Thompson P, Tropak M, Kaytor MD, Keimel JG, Mark BL, Mahuran D, Walia JS, Gray SJ.
Construction of a hybrid β-hexosaminidase subunit capable of forming stable homodimers that hydrolyze GM2 ganglioside in vivo.
Tropak MB, Yonekawa S, Karumuthil-Melethil S, Thompson P, Wakarchuk W, Gray SJ, Walia JS, Mark BL, Mahuran D.
Long-term correction of Sandhoff disease following intravenous delivery of rAAV9 to mouse neonates.
Walia JS, Altaleb N, Bello A, Kruck C, LaFave MC, Varshney GK, Burgess SM, Chowdhury B, Hurlbut D, Hemming R, Kobinger GP, Triggs-Raine B.
Walia JS, Neschadim A, Lopez-Perez O, Alayoubi A, Fan X, Carpentier S, Madden M, Lee CJ, Cheung F, Jaffray DA, Levade T, McCart JA, Medin JA.